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A picture of Payne, an infant with SMA, smiling and holding a gold club, framed inside a 3D object in the shape of the number 1x

The one-time-only dose to stop SMA progression

ZOLGENSMA is a gene therapy for pediatric patients less than 2 years of age with spinal muscular atrophy (SMA) that is delivered as a single-dose, 1-hour infusion. Baseline tests and post-infusion monitoring for at least 3 months after infusion are required. Administration of a systemic corticosteroid before and after infusion is also required.1

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Brady, an infant with SMA, sitting on his mother Nicole's lap

OneGene Program® patient and provider support

"It was amazing to have [the OneGene Program] reach out so quickly because we felt like we had someone in our corner."
— Nicole, Brady’s mom

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References: 1. ZOLGENSMA. Prescribing information. Novartis Gene Therapies, Inc. 2. Glascock J, Sampson J, Haidet-Phillips A, et al. Treatment algorithm for infants diagnosed with spinal muscular atrophy through newborn screening. J Neuromuscul Dis. 2018;5(2):145-158.